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Previous Volume 333:1204-1207 November 2, 1995 Number 18 Next

	Since this article has no abstract, we have provided an extract of the first 100 words of the full text and any section headings.

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Gene therapy is a novel form of drug delivery that enlists the synthetic machinery of the patient's cells to produce a therapeutic agent. Using the body to treat its own disease overcomes the need to manufacture highly purified proteins. It also eliminates the need for repeated parenteral administration of proteins (as in hemophilia) or drugs (as in hereditary hypercholesterolemia) and reduces the difficulties of complying with exogenous-drug regimens. Applications of gene therapy are not limited to rare inherited diseases but extend potentially to common acquired disorders, including cancer, heart disease, and the acquired immunodeficiency syndrome. Gene therapy is thus likely . . . [Full Text of this Article]

Source Information

From the Department of Molecular Pharmacology, Stanford University School of Medicine, Stanford, CA 94305-5332, where reprint requests should be addressed to Dr. Blau.

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